2 results
Approved WMOCompleted
Long-term safety and pharmacokinetics (PK) of neoGAA
Approved WMOPending
The overall objective is to assess efficacy, safety, pharmacokinetic (PK), pharmacodynamics (PD) of avalglucosidase alfa in male and femaleparticipants less than or equal to 6 months of age with IOPD.