2 results
Approved WMOPending
The aims are: (1) to explore the feasibility of XRNT treatment in the Netherlands in terms of treatment participation and treatment retention; and (2) to study the mechanism of action of XRNT using pharmacoMRI and SPECT, and (3) to study the…
Approved WMOWill not start
The purpose of this study is to assess the safety, tolerability and efficacy of long term drisapersen in subjects with DMD.